Targeting the basic defect in cystic fibrosis

N Engl J Med. 2010 Nov 18;363(21):2056-7. doi: 10.1056/NEJMe1010123.
No abstract available

Publication types

  • Editorial
  • Comment

MeSH terms

  • Aminophenols / therapeutic use*
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
  • Humans
  • Infant, Newborn
  • Mutation*
  • Neonatal Screening
  • Quinolones / therapeutic use*

Substances

  • Aminophenols
  • CFTR protein, human
  • Quinolones
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor